Therapeutic Asset Ratings
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Atogepant
Episodic Migraine
Stanford University
P4
A
(87)
Firazyr
Hereditary Angioedema (HAE)
Nang Kuang Pharmaceutical Co., Ltd.
P4
A
(87)
fx-1006a
ATTR-PN
Qilu Pharmaceutical Co., Ltd.
P4
A
(87)
gc1111
Hunter Syndrome
Takeda
P4
A
(86)
Turoctocog Alfa
Congenital Bleeding Disorder
Novo Nordisk A/S
P4
A
(85)
Turoctocog Alfa
Haemophilia A
Novo Nordisk A/S
P4
A
(85)
Eptacog Alfa
Haemophilia A With Inhibitors
AryoGen Pharmed Co.
P4
A
(84)
Factor Ix
Haemophilia B
CSL Behring
P4
A
(84)
Firazyr
Hereditary Angioedema
Nang Kuang Pharmaceutical Co., Ltd.
P4
A
(84)
GLY-GLY-GLY-CYS-TYR-PHE-GLN-ASN-CYS-PRO-LYS-GLY-NH2 (4-9 DISULFIDE)
Hepatorenal Syndrome
Noorik Biopharmaceuticals AG
P4
A
(84)
Recombinant Alpha-Galactosidase A
Fabry Disease
Shire
P4
A
(84)
Sebetralstat
Hereditary Angioedema
KalVista Pharmaceuticals, Ltd.
P4
A
(84)
Velpatasvir
Hepatitis C Virus Infection
Peking University People's Hospital
P4
A
(84)
Acetylsalicylic Acid
Myocardial Infarction
Shanghai CureGene Pharmaceutical Co., Ltd.
P4
A
(83)
Agalsidase Beta
Fabry Disease
Sanofi
P4
A
(83)
Cerezyme
Gaucher Disease, Non-Neuronopathic Form
Sanofi
P4
A
(83)
Duloxetine
Diabetic Neuropathies
Aga Khan University
P4
A
(83)
Edoxaban
Atrial Fibrillation
National Taiwan University Hospital
P4
A
(83)
Lipitor
Dyslipidemia
Johns Hopkins University
P4
A
(83)
Nicotine
Tobacco Use Disorder
Brown University
P4
A
(83)
Velaglucerase Alfa
Gaucher Disease
Takeda
P4
A
(83)
VITAMIN D
Vitamin D Deficiency
Yale University
P4
A
(83)
Alpha-1-Proteinase Inhibitor
Alpha 1-Antitrypsin Deficiency
Grifols Therapeutics LLC
P4
A
(82)
Avalglucosidase Alfa
Glycogen Storage Disease Type II
Genzyme, a Sanofi Company
P4
A
(82)
Cytosin-Arabinosid
Adult Acute Myeloid Leukemia With t(15;17)(q22;q12)
Associazione Italiana Ematologia Oncologia Pediatrica
P4
A
(82)
Showing 1 to 25 of 63,772 assets
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