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Therapeutic Asset Ratings

464 results matching 1 filter

129,767 assets · 8,707 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Sb-Fix
Mucopolysaccharidosis Type 2
Sangamo TherapeuticsD (30)
SIMOLADAGENE AUTOTEMCEL LENTIVIRAL VECTOR
Severe Combined Immunodeficiency, Autosomal Recessive, T Cell-Negative, B Cell-Negative, NK Cell-Negative, Due To Adenosine Deaminase Deficiency
University of California, Los AngelesD (30)
SIMOLADAGENE AUTOTEMCEL LENTIVIRAL VECTOR
Severe Combined Immunodeficiency
University of California, Los AngelesD (30)
Elzocabtagene autoleucel vector (anti-GCC CAR)
Colon Carcinoma
The Affiliated Hospital of Qingdao UniversityN/AD (28)
Temferon
Nonpapillary Renal Cell Carcinoma
Genenta ScienceP1/2D (26)
ICP34.5-, ICP47-DELETED HERPES SIMPLEX VIRUS 1 (HSV-1) INCORPORATING THE HUMAN GM-CSF GENE
Refractory Merkel Cell Carcinoma
National Cancer Institute (NCI)P2NR (0)
ICP34.5-, ICP47-DELETED HERPES SIMPLEX VIRUS 1 (HSV-1) INCORPORATING THE HUMAN GM-CSF GENE
Skin Squamous Cell Carcinoma
National Cancer Institute (NCI)P2NR (0)
ICP34.5-, ICP47-DELETED HERPES SIMPLEX VIRUS 1 (HSV-1) INCORPORATING THE HUMAN GM-CSF GENE
Skin Basal Cell Carcinoma
National Cancer Institute (NCI)P2NR (0)
100 μg ncp-il-22bp mrna
Cancer
West China HospitalP1NR (0)
Kk-Lc-1 Tcr
Kita-kyushu Lung Cancer Antigen 1, Human
National Cancer Institute (NCI)P1NR (0)
crg003
Glycogen Storage Disease Due To Acid Maltase Deficiency, Late-Onset
Huashan HospitalEarly P1NR (0)
Artegene Drug Product
Severe Combined Immunodeficiency Due To DCLRE1C Deficiency
Assistance Publique - Hôpitaux de ParisP1/2NR (0)
Gt-Ugt1A1-Aav8-02
Crigler-Najjar Syndrome Type 1
Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of HealthcareP1/2NR (0)
st002
NF2-Related Schwannomatosis
Cancer Institute and Hospital, Chinese Academy of Medical SciencesN/ANR (0)
Showing 451 to 464 of 464 assets
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