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Therapeutic Asset Ratings

464 results matching 1 filter

129,767 assets · 8,707 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
High Dose Lx2006
Friedreich Ataxia
Lexeo TherapeuticsP1/2CC (47)
lnp1265
Hemophilia B
Regeneron PharmaceuticalsP1/2CC (47)
Low Dose Lx2006
Friedreich Ataxia
Lexeo TherapeuticsP1/2CC (47)
Quaratusugene Ozeplasmid
Small Cell Lung Carcinoma
Genprex, Inc.P1/2CC (47)
Regv131
Hemophilia B
Regeneron PharmaceuticalsP1/2CC (47)
Tilt-123
Fallopian Tube Carcinoma
TILT Biotherapeutics Ltd.P1/2CC (47)
Tilt-123
Primary Peritoneal Carcinoma
TILT Biotherapeutics Ltd.P1/2CC (47)
Vgn-R08B
Parkinson Disease
Shanghai Vitalgen BioPharma Co., Ltd.P1/2CC (47)
GENETICALLY-MODIFIED ONCOLYTIC TYPE 5 ADENOVIRUS WHICH SELECTIVELY REPLICATES IN TUMOR CELLS CONTAINING DYSFUNCTIONAL P53 GENE (H101)
Pancreatic Neoplasm
Fudan UniversityP2CC (46)
Sleeping Beauty Transposed Pbl
Breast Cancer
National Cancer Institute (NCI)P2CC (46)
Sleeping Beauty Transposed Pbl
Non-Small Cell Lung Carcinoma
National Cancer Institute (NCI)P2CC (46)
Sleeping Beauty Transposed Pbl
Ovarian Cancer
National Cancer Institute (NCI)P2CC (46)
Recombinant Hgm-Csf Herpes Simplex Virus
Melanoma
Peking University Cancer Hospital & InstituteP1CC (46)
ab-1001 gene therapy
Huntington Disease
AskBio France, SAS, a subsidiary of AskBio Inc.P1/2CC (45)
Adv/Hsv-Tk
Anaplastic Astrocytoma
The Methodist Hospital Research InstituteP1/2CC (45)
als20
Beta Thalassemia
Children's Hospital of PhiladelphiaP1/2CC (45)
Askbio009
Hemophilia B
Baxalta now part of ShireP1/2CC (45)
DNA (RECOMBINANT REPLICATION-DEFICIENT ADENO-ASSOCIATED VIRUS 5 VECTOR AMT-130 CHICKEN .BETA.-ACTIN PROMOTER PLUS HUMAN HUNTINGTIN MRNA-TARGETING MICRORNA MIHTT-SPECIFYING)
Huntington Disease
UniQure Biopharma B.V.P1/2CC (45)
kxv01 tcr lentinvivo
Cancer
Cancer Institute and Hospital, Chinese Academy of Medical SciencesP1/2CC (45)
Lentivirus Vector Rhiv7-Shi-Tar-Ccr5Rz-Transduced Hematopoietic Stem/Progenitor Cells
Mature T-Cell And NK-Cell Non-Hodgkin Lymphoma
AIDS Malignancy ConsortiumP1/2CC (45)
m032
Anaplastic Astrocytoma
University of Alabama at BirminghamP1/2CC (45)
m032
Gliosarcoma
University of Alabama at BirminghamP1/2CC (45)
oh2
Digestive System Cancer
Binhui Biopharmaceutical Co., Ltd.P1/2CC (45)
oh2
Neoplasm
Binhui Biopharmaceutical Co., Ltd.P1/2CC (45)
Pelareorep
Malignant Pancreatic Neoplasm
Oncolytics BiotechP1/2CC (45)
Showing 201 to 225 of 464 assets
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