Therapeutic Asset Ratings
131 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Inclisiran
Acute Coronary Syndrome
Novartis Pharmaceuticals
P3
B
(60)
Inclisiran
Atherosclerotic Cardiovascular Disease
Novartis Pharmaceuticals
P3
B
(60)
Nucresiran
hATTR-PN
Alnylam Pharmaceuticals
P3
B
(60)
Sepofarsen
Neurologic Manifestations
Laboratoires Thea
P2/3
B
(59)
Olaptesed Pegol
Metastatic Pancreatic Cancer
TME Pharma AG
P2
B
(58)
Tilsotolimod
Malignant Melanoma
A.J.M. van den Eertwegh
P2
B
(58)
Mtl-Cebpa
Hepatitis B
Mina Alpha Limited
P2
B
(57)
Mtl-Cebpa
Hepatitis C
Mina Alpha Limited
P2
B
(57)
RNA, (Am-sp-(2?-deoxy-2?-fluoro)G-sp-Am-Um-Am-Gm-(3??3?)-[1-de-?-D-ribofuranosyl-1-[(2S)-2,3-dihydroxypropyl]]m5U-(2??5?)-Cm-Cm-Am-Um-Gm-Cm-(2?-deoxy-2?-fluoro)A-Am-(2?-deoxy-2?-fluoro)A-Am-Gm-Cm-Am-Um-sp-Um-sp-Cm), complex with RNA (Am-sp-Um-sp-Gm-Cm-Um-Um-(2?-deoxy-2?-fluoro)U-Um-(2?-deoxy-2?-fluoro)G-(2?-deoxy-2?-fluoro)C-(2?-deoxy-2?-fluoro)A-Um-Gm-Gm-Am-Cm-Um-Am-Um-Cm-Um) 3?-[[(2S,4R)-1-[29-[[2-(acetylamino)-2-deoxy-?-D-galactopyranosyl]oxy]-14,14-bis[[3-[[3-[[5-[[2-(acetylamino)-2-deoxy-?-D-galactopyranosyl]oxy]-1-oxopentyl]amino]propyl]amino]-3-oxopropoxy]methyl]-1,12,19,25-tetraoxo-16-oxa-13,20,24-triazanonacos-1-yl]-4-hydroxy-2-pyrrolidinyl]methyl hydrogen phosphate] (1:1)
Metabolic Dysfunction-Associated SteatoHepatitis (MASH)
Regeneron Pharmaceuticals
P2
B
(57)
Mtl-Cebpa
Hepatocellular Carcinoma
Mina Alpha Limited
P2
CCC
(55)
bp1001
Acute Myeloid Leukemia
Bio-Path Holdings, Inc.
P2
CCC
(54)
all-P-ambo-2'-O-(2-methoxyethyl)-5-methyl-P-thiocytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methylcytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-P-thioguanylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-P-thiouridylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-Pthiouridylyl-( 3'?5')-P-thiothymidylyl-(3'?5')-P-thiothymidylyl-(3'?5')-2'-deoxy-5-methyl-P-thiocytidylyl-(3'?5')-Pthiothymidylyl-( 3'?5')-P-thiothymidylyl-(3'?5')-2'-deoxy-Pthioadenylyl-( 3'?5')-2'-deoxy-5-methyl-P-thiocytidylyl-(3'?5')-2'-deoxy-5-methyl-P-thiocytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-Pthioadenylyl-( 3'?5')-2'-O-(2-methoxyethyl)-5-methylcytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-P-thiocytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-P-thiocytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyluridine
Mild Cognitive Impairment Due to Alzheimer's Disease
Biogen
P2
CCC
(53)
Avicursen
Duchenne Muscular Dystrophy
Percheron Therapeutics
P2
CCC
(53)
Cldn6 Rna-Lpx
Extragonadal Germ Cell Tumor
BioNTech SE
P2
CCC
(53)
Cldn6 Rna-Lpx
Testicular Germ Cell Tumor
BioNTech SE
P2
CCC
(53)
Mivelsiran
Down Syndrome-Associated Alzheimer's Disease (DS-AD)
Alnylam Pharmaceuticals
P2
CCC
(53)
Nusinersen
Anti-myostatin
Scholar Rock, Inc.
P2
CCC
(53)
Nusinersen
Neuromuscular Manifestations
Scholar Rock, Inc.
P2
CCC
(53)
Nusinersen
Spinal Muscular Atrophy Type 2
Scholar Rock, Inc.
P2
CCC
(53)
Nusinersen
Spinal Muscular Atrophy Type 3
Scholar Rock, Inc.
P2
CCC
(53)
Vidutolimod
Melanoma
National Cancer Institute (NCI)
P2/3
CCC
(52)
Defibrotide
Sickle Cell Disease
New York Medical College
P2
CCC
(51)
rct2100
Cystic Fibrosis
ReCode Therapeutics
P2
CCC
(51)
DNA, D(3'-AMINO-3'-DEOXY-P-THIO)(T-A-G-G-G-T-T-A-G-A-C-A-A), 5'-(O-(2-HYDROXY-3-((1-OXOHEXADECYL)AMINO)PROPYL) HYDROGEN PHOSPHOROTHIOATE)
Acute Myeloid Leukemia
Douglas Tremblay
P2
CCC
(50)
Nelitolimod
Angiosarcoma
QuantumLeap Healthcare Collaborative
P2
CCC
(50)
Showing 26 to 50 of 131 assets
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