Therapeutic Asset Ratings
2,394 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Turoctocog Alfa
Congenital Bleeding Disorder
Novo Nordisk A/S
P4
A
(85)
Turoctocog Alfa
Haemophilia A
Novo Nordisk A/S
P4
A
(85)
GLY-GLY-GLY-CYS-TYR-PHE-GLN-ASN-CYS-PRO-LYS-GLY-NH2 (4-9 DISULFIDE)
Hepatorenal Syndrome
Noorik Biopharmaceuticals AG
P4
A
(84)
Recombinant Alpha-Galactosidase A
Fabry Disease
Shire
P4
A
(84)
Agalsidase Beta
Fabry Disease
Sanofi
P4
A
(83)
Velaglucerase Alfa
Gaucher Disease
Takeda
P4
A
(83)
Avalglucosidase Alfa
Glycogen Storage Disease Type II
Genzyme, a Sanofi Company
P4
A
(82)
.ALPHA.-1 PROTEASE INHIBITOR
Alpha 1-Antitrypsin Deficiency
Grifols Therapeutics LLC
P4
A
(81)
PHENYLASE
Phenylketonuria (PKU)
BioMarin Pharmaceutical
P4
A
(81)
Semaglutide
Metabolism and Nutrition Disorder
Nordsjaellands Hospital
P4
A
(81)
Setmelanotide
Bardet Biedl Syndrome (BBS)
Tom Hühne
P4
A
(81)
Alglucosidase Alfa
Pompe Disease
Erasmus Medical Center
P4
A
(80)
Avalglucosidase Alfa
Pompe Disease
Genzyme, a Sanofi Company
P4
A
(80)
Rasburicase
Tumor Lysis Syndrome
M.D. Anderson Cancer Center
P4
A
(80)
Nonacog Beta Pegol
Haemophilia B
Novo Nordisk A/S
P3
A
(80)
Pegunigalsidase Alfa
Fabry Disease
Chiesi Italia
P3
A
(80)
Glatiramer
Relapsing Remitting Multiple Sclerosis
University Hospital, Montpellier
P4
BBB
(79)
Liraglutide
PCOS
Peking University Third Hospital
P4
BBB
(79)
Liraglutide
Type 1 Diabetes
Dasman Diabetes Institute
P4
BBB
(79)
Liraglutide
Type 2 Diabetes Mellitus
RenJi Hospital
P4
BBB
(79)
Rurioctocog Alfa Pegol
Hemophilia A
Takeda
P4
BBB
(79)
Semaglutide
Diabetes Mellitus, Type 2
Shanghai Jiao Tong University School of Medicine
P4
BBB
(79)
Semaglutide
PCOS
Methodist Health System
P4
BBB
(79)
Alglucosidase Alfa
Pompe Disease (Late-onset)
Erasmus Medical Center
P4
BBB
(78)
ASPARAGINASE
Adult Acute Lymphocytic Leukemia
Institute of Hematology & Blood Diseases Hospital, China
P4
BBB
(78)
Showing 1 to 25 of 2,394 assets
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