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Therapeutic Asset Ratings

146 results matching 1 filter

133,990 assets · 8,802 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Cald Hr-D
Globoid Cell Leukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Glycoprotein Metabolic Disorders
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation)
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Hunter Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Hurler Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Infantile Refsum Disease
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Inherited Metabolic Disorders
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Maroteaux Lamy Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Metachromatic Leukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Mitochondrial Neurogastrointestingal Encephalopathy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Mucopolysaccharidosis Disorders
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Multifunctional Enzyme Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Neonatal Adrenoleukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Niemann-Pick B
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Niemann-Pick C Subtype 2
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Peroxisomal Disorders
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Recessive Leukodystrophies
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Severe Osteopetrosis
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Sly Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Sphingolipidoses
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Sphingomyelin Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Zellweger Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Polymer-Lipid Nanoparticle-Mediated Delivery Of Cd19/Cd20 Dual-Targeting Invivocar1920 Mrna For Car-T Cell Immunotherapy
B-cell Lymphoma Refractory
Daihong LiuP2CCC (53)
Tas-102
Advanced Lymphoma
National Cancer Institute (NCI)P2CCC (53)
Tas-102
Advanced Malignant Solid Neoplasm
National Cancer Institute (NCI)P2CCC (53)
Showing 51 to 75 of 146 assets
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