Therapeutic Asset Ratings
7,407 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Berotralstat
Hereditary Angioedema
BioCryst Pharmaceuticals
P3
A
(82)
Lanadelumab
Hereditary Angioedema (HAE)
Takeda
P3
A
(80)
Nonacog Beta Pegol
Haemophilia B
Novo Nordisk A/S
P3
A
(80)
Pegunigalsidase Alfa
Fabry Disease
Chiesi Italia
P3
A
(80)
Migalastat
Fabry Disease
Amicus Therapeutics
P3
BBB
(79)
Cytosin-Arabinosid
Adult Acute Monoblastic Leukemia (M5a)
Chinese PLA General Hospital
P3
BBB
(78)
Cytosin-Arabinosid
Adult Acute Myeloblastic Leukemia Without Maturation (M1)
Northwestern University
P3
BBB
(78)
Cytosin-Arabinosid
Adult Acute Myelomonocytic Leukemia (M4)
University of Alberta
P3
BBB
(78)
Cytosin-Arabinosid
Untreated Childhood Acute Myeloid Leukemia and Other Myeloid Malignancies
Children's Oncology Group
P3
BBB
(78)
Daunorubicin
Untreated Adult Acute Myeloid Leukemia
Wake Forest University Health Sciences
P3
BBB
(78)
Deucrictibant
C1 Esterase Inhibitor Deficiency
Institute for Asthma and Allergy
P3
BBB
(78)
Deucrictibant
C1 Inhibitor Deficiency
Institute for Asthma and Allergy
P3
BBB
(78)
Deucrictibant
Hereditary Angioedema With C1 Esterase Inhibitor Deficiency
Institute for Asthma and Allergy
P3
BBB
(78)
Immunoglobulin G4 [230-proline,de-449-lysine], anti-(human blood-coagulation factor IX)(human clone 0365-0001-9985 ?4-chain), disulfide with human clone 0365-0001-9985 ?-chain, (228?226?),(231?229?)-bis(disulfide) with anti-(human blood-coagulation factor X) immunoglobulin G4 [228-proline,405-leucine,409-lysine,de-447-lysine] (human clone 0365-0001-8174 ?4-chain) disulfide with human clone 0365-0001-8174 ?-chain
Haemophilia A
Novo Nordisk A/S
P3
BBB
(78)
PABINAFUSP ALFA
Mucopolysaccharidosis II
JCR Pharmaceuticals Co., Ltd.
P3
BBB
(78)
Turoctocog Alfa Pegol
Haemophilia A
Novo Nordisk A/S
P3
BBB
(78)
Calcium folinate pentahydrate
Stage IV Colon Cancer
Sun Yat-sen University
P3
BBB
(77)
CIS-DIAMMINEDICHLOROPLATINUM II
Primary Peritoneal Cavity Cancer
GOG Foundation
P3
BBB
(77)
Daunorubicin
Adult Acute Monoblastic Leukemia (M5a)
National Cancer Institute (NCI)
P3
BBB
(77)
Daunorubicin
Adult Acute Myeloblastic Leukemia Without Maturation (M1)
National Cancer Institute (NCI)
P3
BBB
(77)
Daunorubicin
Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities
National Cancer Institute (NCI)
P3
BBB
(77)
Daunorubicin
Adult Acute Myelomonocytic Leukemia (M4)
National Cancer Institute (NCI)
P3
BBB
(77)
Eloxatin
Colon Adenocarcinoma
Sun Yat-sen University
P3
BBB
(77)
ETOPOSIDE
Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities
M.D. Anderson Cancer Center
P3
BBB
(77)
ETOPOSIDE
Adult Acute Myeloid Leukemia With Del(5q)
Alice Mims
P3
BBB
(77)
Showing 1 to 25 of 7,407 assets
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