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Therapeutic Asset Ratings

705 results matching 1 filter

129,767 assets · 8,707 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Busulphan
Mitochondrial Neurogastrointestingal Encephalopathy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Monosomy 7 Myelodysplasia And Leukemia Syndrome 1
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Multifunctional Enzyme Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Natural Killer Cell Malignancies
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Neonatal Adrenoleukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Neurofibromatosis Type 1
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
NF1 Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Niemann-Pick B
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Niemann-Pick C Subtype 2
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
N-RAS Gene Amplification
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
PTPN11 Gene Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Recessive Leukodystrophies
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Somatic Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Sphingomyelin Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
T Cell Receptor Alpha/Beta Depletion
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Dyskeratosis Congenita And Related Telomere Biology Disorder
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Li-Fraumeni Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Busulphan
Zellweger Syndrome
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Peroxisomal Acyl-CoA Oxidase Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
X-Linked Cerebral Adrenoleukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Alpha-Mannosidosis
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Alpha-Methylacyl-CoA Racemase Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Aspartylglucosaminuria
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
D-Bifunctional Protein Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Cald Hr-D
Fucosidosis
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Showing 226 to 250 of 705 assets
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