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Therapeutic Asset Ratings

705 results matching 1 filter

129,767 assets · 8,707 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Fludarabine
Adrenoleukodystrophy With Cerebral Involvement
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Alpha-methylacyl-CoA Racmase Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
CBL-Related Disorder
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Central Nervous System Leukemia
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Chromosomal Disorder
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
D-Bifunctional Enzyme Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Hereditary Persistence Of Fetal Hemoglobin
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Glycoprotein Metabolic Disorders
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Transplant Rejection
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation)
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Infantile Refsum Disease
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
B-Lymphoblastic Leukemia/Lymphoma With IAMP21
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Mitochondrial Neurogastrointestingal Encephalopathy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Monosomy 7 Myelodysplasia And Leukemia Syndrome 1
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Multifunctional Enzyme Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Neonatal Adrenoleukodystrophy
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Neurofibromatosis Type 1
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
NF1 Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Niemann-Pick B
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Niemann-Pick C Subtype 2
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
N-RAS Gene Amplification
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
PTPN11 Gene Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Recessive Leukodystrophies
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Somatic Mutation
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Fludarabine
Sphingomyelin Deficiency
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Showing 351 to 375 of 705 assets
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