Therapeutic Asset Ratings
153 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Busulphan
Systemic Juvenile Idiopathic Arthritis (sJIA)
Paul Szabolcs
P2
CCC
(53)
Cyclophosphamide
Hereditary Anemias
Paul Szabolcs
P2
CCC
(53)
Cyclophosphamide
Inflammatory Conditions
Paul Szabolcs
P2
CCC
(53)
Cyclophosphamide
Juvenile Rheumatoid Arthritis
Paul Szabolcs
P2
CCC
(53)
Cyclophosphamide
Systemic Juvenile Idiopathic Arthritis (sJIA)
Paul Szabolcs
P2
CCC
(53)
Evomela
CD40 Deficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
CD40 Ligand Deficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
Chronic Granulomatous Disease
Paul Szabolcs
P2
CCC
(53)
Evomela
Common Variable Immune Deficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
Congenital Bone Marrow Failure Syndromes
Paul Szabolcs
P2
CCC
(53)
Evomela
DiGeorge Syndrome
Paul Szabolcs
P2
CCC
(53)
Evomela
GATA2 Associated Immunodeficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
Hereditary Anemias
Paul Szabolcs
P2
CCC
(53)
Evomela
Hypomorphic RAG1 Deficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
Hypomorphic RAG2 Deficiency
Paul Szabolcs
P2
CCC
(53)
Evomela
Immune Dysregulation
Paul Szabolcs
P2
CCC
(53)
Evomela
Inflammatory Conditions
Paul Szabolcs
P2
CCC
(53)
Evomela
IPEX
Paul Szabolcs
P2
CCC
(53)
Evomela
Juvenile Rheumatoid Arthritis (JRA)
Paul Szabolcs
P2
CCC
(53)
Evomela
Mendelian Susceptibility to Mycobacterial Disease
Paul Szabolcs
P2
CCC
(53)
Evomela
Omenn Syndrome
Paul Szabolcs
P2
CCC
(53)
Evomela
Primary Immune Deficiency Disorder
Paul Szabolcs
P2
CCC
(53)
Evomela
STAT 1 Gain of Function
Paul Szabolcs
P2
CCC
(53)
Evomela
STAT 3 Gain of Function
Paul Szabolcs
P2
CCC
(53)
Evomela
Systemic Juvenile Idiopathic Arthritis (sJIA)
Paul Szabolcs
P2
CCC
(53)
Showing 26 to 50 of 153 assets
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