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Therapeutic Asset Ratings

91,564 assets7,904 sponsors3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Aoc 1044
Duchenne Muscular Dystrophy
Avidity Biosciences, Inc.P3BB (70)
ask120067
Non-Small Cell Lung Carcinoma
Jiangsu Aosaikang Pharmaceutical Co., Ltd.P3BB (70)
Atumelnant
Classic Congenital Adrenal Hyperplasia
Crinetics Pharmaceuticals Inc.P3BB (70)
Atumelnant
Congenital Adrenal Hyperplasia
Crinetics Pharmaceuticals Inc.P3BB (70)
Autologous Cd34+ Cells Isolated From Mobilised Peripheral Blood By Positive Selection, Modified By Crispr/Cas9 (Clustered Regularly Interspaced Short Palindromic Repeats/Crispr-Associated Protein 9) Mediated Gene Editing Consisting Of A Guide Rna (Grna) Introduced Transiently As Ribonucleoprotein (Rnp) Complex, Targeting The Erythroid Lineage-Specific Enhancer Region Of Bcl11A (B-Cell Lymphoma/Leukemia 11A). The Site-Specific Cleavage By Cas9 Forms A Double Strand Break (Dsb), Which Is Subsequently Repaired By Nonhomologous End-Joining (Nhej), Leading To The Transcriptional Repression Of Bcl11A, A Repressor Of ?-Globin Gene Transcription
Hematologic Disorder
Vertex Pharmaceuticals IncorporatedP3BB (70)
Axs-05
Alzheimer Disease
Axsome Therapeutics, Inc.P3BB (70)
Bendamustine
B-Cell Chronic Lymphocytic Leukemia
Mayo ClinicP3BB (70)
Bendamustine
Non-Hodgkin Lymphoma
MEI Pharma, Inc.P3BB (70)
Bexicaserin
Developmental And Epileptic Encephalopathy
Longboard PharmaceuticalsP3BB (70)
Brentuximab Vedotin
Primary Cutaneous T-Cell Non-Hodgkin Lymphoma
Assistance Publique - Hôpitaux de ParisP3BB (70)
Brivaracetam
Epilepsy
Jiangsu Chia Tai Fenghai Pharmaceutical Co., Ltd.P3BB (70)
Busulfanum
Acute Myeloid Leukemia With 11q23 Abnormalities
M.D. Anderson Cancer CenterP3BB (70)
Busulfanum
Childhood Acute Myeloid Leukemia
Washington University School of MedicineP3BB (70)
Busulfanum
Diffuse Large B-Cell Lymphoma
Sichuan UniversityP3BB (70)
Busulfanum
Disease Related To Transplantation
M.D. Anderson Cancer CenterP3BB (70)
Cabozantinib
Castration-Resistant Prostate Carcinoma
Rana McKay, MDP3BB (70)
Calaspargase Pegol
Lymphoblastic Lymphoma
Children's Oncology GroupP3BB (70)
Capecitabine
Diffuse Large B-Cell Lymphoma
GenmabP3BB (70)
Capecitabine
Gallbladder Cancer
Merck Sharp & Dohme LLCP3BB (70)
Capecitabine
Rectal Cancer
Tao ZhangP3BB (70)
Capecitabine
Gastric Neoplasm
SUNHO(China)BioPharmaceutical CO., Ltd.P3BB (70)
Carboplatin
Fallopian Tube Clear Cell Adenocarcinoma
NRG OncologyP3BB (70)
Carboplatin
Fallopian Tube Endometrioid Adenocarcinoma
National Cancer Institute (NCI)P3BB (70)
Carboplatin
Fallopian Tube Neoplasm
Eli Lilly and CompanyP3BB (70)
Carboplatin
Hormone Receptor-Positive Breast Cancer
Avenzo Therapeutics, Inc.P3BB (70)
Showing 1401 to 1425 of 42,327 assets
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