Therapeutic Asset Ratings
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91,564
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3,128
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Asset
Sponsor
Phase
Rating
Decitabine
Acute Undifferentiated Leukemia
Fred Hutchinson Cancer Center
P1/2
CC
(47)
Defactinib
Malignant Glioma
Institute of Cancer Research, United Kingdom
P1/2
CC
(47)
Dexasone
Corneal Disorder
Hellenic Society of Hematology
P1/2
CC
(47)
Disialoganglioside Gd-2
B-Cell Non-Hodgkin Lymphoma
Shenzhen Geno-Immune Medical Institute
P1/2
CC
(47)
dji136
Small Cell Lung Carcinoma
Novartis Pharmaceuticals
P1/2
CC
(47)
Dna (Recombinant Adeno-Associated Virus Vector Aav-Spark100-Gaa Human Liver-Specific Expression Cassette Including Human Lysosomal ?-Glucosidase Codon-Optimized Gene Gaa Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks)
Glycogen Storage Disease II
Spark Therapeutics, Inc.
P1/2
CC
(47)
Dna (Recombinant Adeno-Associated Virus Vector Aav-Spark100-Gaa Human Liver-Specific Expression Cassette Including Human Lysosomal ?-Glucosidase Codon-Optimized Gene Gaa Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks)
Glycogen Storage Disease Due To Acid Maltase Deficiency, Late-Onset
Spark Therapeutics, Inc.
P1/2
CC
(47)
Dna (Recombinant Human Hematopoietic Stem Cell-Derived Adeno-Associated Virus Vector Serotype Aavhsc15 Human Liver-Specific Expression Cassette Including Human Phenylalanine 4-Hydroxylase Codon-Optimized Cdna Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks)
Phenylketonuria
Homology Medicines, Inc
P1/2
CC
(47)
Dna (Recombinant Replication-Defective Adeno-Associated Virus Serotype 9 Vector Ux701 Murine Transthyretin Enhancer Plus Human Transthyretin Promoter Plus Simian Virus 40 Intron Plus Human Adenosine Triphosphatase Copper-Transporting ? Metal-Binding Domain 4/5/6 Transgene Atp7B-Mbd456 Plus Simian Virus 40 Polyadenylation Signal Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks Plus Adeno-Associated Virus 2 Rep Region Plus Adeno-Associated Virus 9 Cap Region-Specifying)
Wilson Disease
Ultragenyx Pharmaceutical Inc
P1/2
CC
(47)
Dna (Recombinant Replication-Deficient Adeno-Associated Virus 5 Vector Bmn 307 Human Liver-Specific Transcription Regulatory Element Plus Human Phenylalanine 4-Hydroxylase Codon-Optimized Gene Hpah Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks)
Phenylketonuria
BioMarin Pharmaceutical
P1/2
CC
(47)
dnl593
Frontotemporal Dementia
Denali Therapeutics Inc.
P1/2
CC
(47)
Docetaxel
Adenoid Cystic Carcinoma
National Cancer Institute (NCI)
P1/2
CC
(47)
Docetaxel
Cervical Squamous Cell Carcinoma
Hummingbird Bioscience
P1/2
CC
(47)
Docetaxel
Liposarcoma
OncoResponse, Inc.
P1/2
CC
(47)
Docetaxel
Malignant Pleural Mesothelioma
NuCana plc
P1/2
CC
(47)
Docetaxel
Salivary Gland Cancer
National Cancer Institute (NCI)
P1/2
CC
(47)
Dostarlimab
Ependymoma
GlaxoSmithKline
P1/2
CC
(47)
Dostarlimab
Fibrolamellar Hepatocellular Carcinoma
GlaxoSmithKline
P1/2
CC
(47)
Dostarlimab
Hepatoblastoma
GlaxoSmithKline
P1/2
CC
(47)
Dual-Target Antigen-Selected Car-Nk
Colorectal Cancer
Essen Biotech
P1/2
CC
(47)
Dual-Target Car-Nk Cells
Gastric Adenocarcinoma
Beijing Biotech
P1/2
CC
(47)
Dual-Target Car-Nk Cells
Gastroesophageal Junction Adenocarcinoma
Beijing Biotech
P1/2
CC
(47)
Duvalgagene Otiparvovec
Fabry Disease
4D Molecular Therapeutics
P1/2
CC
(47)
Duvelisib
Primary Cutaneous T-Cell Non-Hodgkin Lymphoma
Jonsson Comprehensive Cancer Center
P1/2
CC
(47)
Duvelisib
Melanoma
John Kirkwood
P1/2
CC
(47)
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