Therapeutic Asset Ratings
153 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Asset
Sponsor
Phase
Rating
Busulphan
Diamond-blackfan Anemia
Paul Szabolcs
P2/3
BBB
(72)
FILGRASTIM
Diamond-Blackfan Anemia
Paul Szabolcs
P2/3
BB
(70)
Cyclophosphamide
Diamond-Blackfan Anemia
Paul Szabolcs
P2/3
BB
(68)
IMMUNOGLOBULIN G1 (HUMAN-RAT MONOCLONAL CAMPATH-1H .GAMMA.1-CHAIN ANTI-HUMAN ANTIGEN CD52), DISULFIDE WITH HUMAN-RAT MONOCLONAL CAMPATH-1H LIGHT CHAIN, DIMER
Diamond-blackfan Anemia
Paul Szabolcs
P2
B
(62)
Cyclophosphamide
Idiopathic Pulmonary Fibrosis
Paul Szabolcs
P3
B
(59)
Fludarabine
Congenital Immunodeficiency
Paul Szabolcs
P2
B
(57)
Fludarabine
GATA2 Associated Immunodeficiency
Paul Szabolcs
P2
B
(57)
Anti-Thymoglobulin, Rabbit
CD40 Deficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
CD40 Ligand Deficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Chronic Granulomatous Disease
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Common Variable Immunodeficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
DiGeorge Syndrome
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
GATA2 Associated Immunodeficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Hypomorphic RAG1 Deficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Hypomorphic RAG2 Deficiency
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Immune Dysregulation
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Immune Dysregulation Polyendocrinopathy Enteropathy X-Linked Syndrome
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Mendelian Susceptibility to Mycobacterial Disease
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Omenn Syndrome
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
Primary Immune Regulatory Disorder
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
STAT 1 Gain of Function
Paul Szabolcs
P2
CCC
(53)
Anti-Thymoglobulin, Rabbit
STAT 3 Gain of Function
Paul Szabolcs
P2
CCC
(53)
Busulphan
Hereditary Anemias
Paul Szabolcs
P2
CCC
(53)
Busulphan
Inflammatory Conditions
Paul Szabolcs
P2
CCC
(53)
Busulphan
Juvenile Rheumatoid Arthritis (JRA)
Paul Szabolcs
P2
CCC
(53)
Showing 1 to 25 of 153 assets
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