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Therapeutic Asset Ratings

153 results matching 1 filter

133,990 assets · 8,802 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
Busulphan
Diamond-blackfan Anemia
Paul SzabolcsP2/3BBB (72)
FILGRASTIM
Diamond-Blackfan Anemia
Paul SzabolcsP2/3BB (70)
Cyclophosphamide
Diamond-Blackfan Anemia
Paul SzabolcsP2/3BB (68)
IMMUNOGLOBULIN G1 (HUMAN-RAT MONOCLONAL CAMPATH-1H .GAMMA.1-CHAIN ANTI-HUMAN ANTIGEN CD52), DISULFIDE WITH HUMAN-RAT MONOCLONAL CAMPATH-1H LIGHT CHAIN, DIMER
Diamond-blackfan Anemia
Paul SzabolcsP2B (62)
Cyclophosphamide
Idiopathic Pulmonary Fibrosis
Paul SzabolcsP3B (59)
Fludarabine
Congenital Immunodeficiency
Paul SzabolcsP2B (57)
Fludarabine
GATA2 Associated Immunodeficiency
Paul SzabolcsP2B (57)
Anti-Thymoglobulin, Rabbit
CD40 Deficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
CD40 Ligand Deficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Chronic Granulomatous Disease
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Common Variable Immunodeficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
DiGeorge Syndrome
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
GATA2 Associated Immunodeficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Hypomorphic RAG1 Deficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Hypomorphic RAG2 Deficiency
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Immune Dysregulation
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Immune Dysregulation Polyendocrinopathy Enteropathy X-Linked Syndrome
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Mendelian Susceptibility to Mycobacterial Disease
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Omenn Syndrome
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
Primary Immune Regulatory Disorder
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
STAT 1 Gain of Function
Paul SzabolcsP2CCC (53)
Anti-Thymoglobulin, Rabbit
STAT 3 Gain of Function
Paul SzabolcsP2CCC (53)
Busulphan
Hereditary Anemias
Paul SzabolcsP2CCC (53)
Busulphan
Inflammatory Conditions
Paul SzabolcsP2CCC (53)
Busulphan
Juvenile Rheumatoid Arthritis (JRA)
Paul SzabolcsP2CCC (53)
Showing 1 to 25 of 153 assets
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