(1,1'-BIPHENYL)-3-CARBOXYLIC ACID, 2',4'-DIFLUORO-4-HYDROXY-
Familial Amyloid Polyneuropathy
Boston UniversitySmall moleculePhase 2/3Dormant
B
61/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 46/ 100
- Competitive Position
- 95/ 100
Competitive context
10 Active assets in the Familial Amyloid Polyneuropathy cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
fx-1006a Qilu Pharmaceutical Co., Ltd. | Phase 4 | A |
fx-1006a Pfizer | Phase 4 | BBB |
Tegsedi Akcea Therapeutics | Phase 4 | BB |
Revusiran Alnylam Pharmaceuticals | Phase 3 | BB |
fx-1006a Qilu Pharmaceutical Co., Ltd. | Phase 4 | BB |
View all 18 →
Same molecule, other indications
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