ACETIC ACID, SODIUM SALT (1:1)
Tuberous Sclerosis Complex
Brigham and Women's HospitalSmall moleculePhase 1/2Active
CCC
48/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 33/ 100
- Competitive Position
- 95/ 100
Competitive context
4 Active assets in the Tuberous Sclerosis Complex cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Everolimus Hospices Civils de Lyon | Phase 3 | BBB |
Ganaxolone Marinus Pharmaceuticals | Phase 3 | BB |
Npc-12Y Gel Nobelpharma | Phase 3 | BB |
gwp42003-p Jazz Pharmaceuticals | Phase 3 | BB |
Vigabatrin Katarzyna Kotulska | Phase 2/3 | BB |
View all 9 →
Same molecule, other indications
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