at2221
Pompe Disease
Amicus TherapeuticsPhase 1/2Dormant
CCC
50/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 37/ 100
- Competitive Position
- 89/ 100
Competitive context
9 Active assets in the Pompe Disease cohort.
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Same molecule, other indications
at2221 is also rated in:
glycogen storage disease due to acid maltase deficiency, late-onsetDormant
B
Indicative ·
62 / 100
View asset →glycogen storage disease due to acid maltase deficiency, infantile onsetDormant
D
Indicative ·
30 / 100
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