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AUTOLOGOUS CD34+ CELLS ENCODING .BETA.A-T87Q-GLOBIN GENE

Fabry Disease

AVROBIOCell therapyDormant
D
30/ 100
Provisional rating · Methodology v0.2

Rating breakdown

Clinical Evidence
15/ 100
Competitive Position
89/ 100

Competitive context

15 Active assets in the Fabry Disease cohort.

Asset / SponsorPhaseRating
Recombinant Alpha-Galactosidase A
Shire
Phase 4A
Agalsidase Beta
Sanofi
Phase 4A
Pegunigalsidase Alfa
Chiesi Italia
Phase 3A
Migalastat
Amicus Therapeutics
Phase 3BBB
Lucerastat
Idorsia Pharmaceuticals Ltd.
Phase 3BB

View all 29 →

Same molecule, other indications

AUTOLOGOUS CD34+ CELLS ENCODING .BETA.A-T87Q-GLOBIN GENE is also rated in:

beta thalassemiaDormant
B
Indicative ·
60 / 100
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beta-thalassemia majorDormant
CCC
Indicative ·
55 / 100
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Transfusion-dependent Beta-ThalassemiaDormant
CCC
Indicative ·
55 / 100
View asset →

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