Floatz logo

AUTOLOGOUS CD34+ CELLS ENCODING .BETA.A-T87Q-GLOBIN GENE

Fanconi Anemia

Rocket Pharmaceuticals Inc.Cell therapyActive
D
30/ 100
Provisional rating · Methodology v0.2

Rating breakdown

Clinical Evidence
15/ 100
Competitive Position
95/ 100

Competitive context

19 Active assets in the Fanconi Anemia cohort.

Asset / SponsorPhaseRating
Cyclophosphamide
Porteus, Matthew, MD
Phase 2/3BBB
Fludarabine
Porteus, Matthew, MD
Phase 2/3BBB
Busulphan
Masonic Cancer Center, University of Minnesota
Phase 2/3BBB
Monomethyl Fumarate
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Phase 2/3BBB
CYCLOSPORIN A
Fred Hutchinson Cancer Center
Phase 2BBB

View all 43 →

Same molecule, other indications

AUTOLOGOUS CD34+ CELLS ENCODING .BETA.A-T87Q-GLOBIN GENE is also rated in:

beta thalassemiaDormant
B
Indicative ·
60 / 100
View asset →
beta-thalassemia majorDormant
CCC
Indicative ·
55 / 100
View asset →
Transfusion-dependent Beta-ThalassemiaDormant
CCC
Indicative ·
55 / 100
View asset →

Need depth?

Order a full diligence report on this asset.

Order report →

Are you the sponsor?

Submit your data room for a Verified Rating. The public-data rating remains visible alongside.

Contact →