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DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS AAVS3-FLT180A VECTOR HUMAN BLOOD-COAGULATION FACTOR IX PADUA-SPECIFYING)

Hemophilia B

Spur Therapeuticsgene_therapyPhase 1/2Dormant
CC
45/ 100
Provisional rating · Methodology v0.2

Rating breakdown

Clinical Evidence
33/ 100
Competitive Position
81/ 100

Competitive context

33 Active assets in the Hemophilia B cohort.

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