Golodirsen
Duchenne Muscular Dystrophy
Rare Disease Research, LLCnucleic_acidPhase 4 / ApprovedActive
BB
70/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 62/ 100
- Competitive Position
- 81/ 100
Competitive context
55 Active assets in the Duchenne Muscular Dystrophy cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Viltolarsen NS Pharma, Inc. | Phase 4 | BBB |
Delandistrogene Moxeparvovec Sarepta Therapeutics, Inc. | Phase 3 | BB |
Aoc 1044 Avidity Biosciences, Inc. | Phase 3 | BB |
Avi-4658 Sarepta Therapeutics, Inc. | Phase 3 | BB |
CHLOROPTIC-P S.O.P. COMPONENT PREDNISOLONE Anne M. Connolly | Phase 4 | BB |
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