ISIS-333611
Familial Amyotrophic Lateral Sclerosis
Ionis Pharmaceuticals, Inc.nucleic_acidPhase 1Dormant
CC
47/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 32/ 100
- Competitive Position
- 95/ 100
Competitive context
0 Active assets in the Familial Amyotrophic Lateral Sclerosis cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Pyrimethamine Weill Medical College of Cornell University | Phase 1/2 | CCC |
BETAMETHASONE Edward Kasaraskis | Early Phase 1 | CC |
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