Monomethyl Fumarate
Congenital Amegakaryocytic Thrombocytopenia
Roswell Park Cancer InstituteSmall moleculePhase 2Dormant
B
57/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 42/ 100
- Competitive Position
- 95/ 100
Competitive context
6 Active assets in the Congenital Amegakaryocytic Thrombocytopenia cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Fludarabine Fred Hutchinson Cancer Center | Phase 2 | BB |
Busulphan University of California, San Francisco | Phase 2 | BB |
METHOTREXATE Fred Hutchinson Cancer Center | Phase 2 | BB |
Thiotepa Fred Hutchinson Cancer Center | Phase 2 | BB |
Romidepsin University of California, San Francisco | Phase 2 | BB |
View all 16 →
Same molecule, other indications
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