Sapablursen
Beta-Thalassemia Intermedia
Ionis Pharmaceuticals, Inc.nucleic_acidPhase 2Dormant
CCC
53/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 38/ 100
- Competitive Position
- 95/ 100
Competitive context
3 Active assets in the Beta-Thalassemia Intermedia cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Sodium 2,2 Dimethylbutyrate Boston University | Phase 2 | B |
Mitapivat Agios Pharmaceuticals, Inc. | Phase 3 | B |
Vit-2763 Twice A Day Vifor (International) Inc. | Phase 2 | B |
Hydroxyurea Shiraz University of Medical Sciences | Phase 2 | B |
Vit-2763 Once A Day Vifor (International) Inc. | Phase 2 | B |
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