Valoctocogene Roxaparvovec
Severe Haemophilia A
BioMarin Pharmaceuticalgene_therapyPhase 1/2Dormant
CCC
52/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 37/ 100
- Competitive Position
- 95/ 100
Competitive context
10 Active assets in the Severe Haemophilia A cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
HUMAN ANTIHEMOPHILIC FACTOR/VON WILLEBRAND FACTOR COMPLEX AryoGen Pharmed Co. | Phase 4 | BBB |
Human-Cl Rhfviii Octapharma | Phase 3 | BBB |
Emicizumab Chulalongkorn University | Phase 4 | BBB |
Rfviiifc Bioverativ Therapeutics Inc. | Phase 3 | BB |
Frsw117 Hangzhou Gensciences Biopharmaceutical Co., Ltd. | Phase 3 | BB |
View all 21 →
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