VOLRUBIGENE RALAPARVOVEC
Crigler-Najjar Syndrome
Audentes Therapeuticsgene_therapyPhase 1Dormant
CC
43/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 28/ 100
- Competitive Position
- 95/ 100
Competitive context
2 Active assets in the Crigler-Najjar Syndrome cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Imlifidase Genethon | Phase 2 | CCC |
gnt0003 Genethon | Phase 2 | CCC |
Orlistat University Medical Center Groningen | N/A | D |
Hepastem Cellaion SA | Phase 1/2 | NR |
Are you the sponsor?
Submit your data room for a Verified Rating. The public-data rating remains visible alongside.
Contact →