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22 assets in Alpha 1-Antitrypsin Deficiency

Therapeutic assets addressing Alpha 1-Antitrypsin Deficiency, rated under Floatz methodology v0.2 and sorted by current rating.

AssetSponsorPhaseRating
Alpha-1-Proteinase Inhibitor
Alpha 1-Antitrypsin Deficiency
Grifols Therapeutics LLCP4A (82)
.Alpha.-1 Protease Inhibitor
Alpha 1-Antitrypsin Deficiency
Grifols Therapeutics LLCP4A (81)
Fazirsiran
Alpha 1-Antitrypsin Deficiency
TakedaP3BB (66)
20-valent pneumococcal conjugate vaccine
Alpha 1-Antitrypsin Deficiency
University of Alabama at BirminghamP4BB (65)
Rymphysia
Alpha 1-Antitrypsin Deficiency
TakedaP4B (60)
sar447537
Alpha 1-Antitrypsin Deficiency
SanofiP2B (57)
Wve-006
Alpha 1-Antitrypsin Deficiency
Wave Life Sciences USA, Inc.P1/2B (57)
vx-864
Alpha 1-Antitrypsin Deficiency
Vertex Pharmaceuticals IncorporatedP2CCC (55)
Belcesiran
Alpha 1-Antitrypsin Deficiency
Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyP2CCC (50)
Tsra-196
Alpha 1-Antitrypsin Deficiency
Tessera Therapeutics, Inc.P1/2CCC (48)
Beam-302
Alpha 1-Antitrypsin Deficiency
Beam Therapeutics Inc.P1/2CC (47)
vx-668
Alpha 1-Antitrypsin Deficiency
Vertex Pharmaceuticals IncorporatedP1CC (47)
vx-634
Alpha 1-Antitrypsin Deficiency
Vertex Pharmaceuticals IncorporatedP1CC (46)
aav8haat
Alpha 1-Antitrypsin Deficiency
Weill Medical College of Cornell UniversityP1CC (43)
Air-001
Alpha 1-Antitrypsin Deficiency
AIRNA CorporationP1CC (43)
Bmn 349
Alpha 1-Antitrypsin Deficiency
BioMarin PharmaceuticalP1CC (43)
kb408
Alpha 1-Antitrypsin Deficiency
Krystal Biotech, Inc.P1CC (43)
Yolt-202
Alpha 1-Antitrypsin Deficiency
RenJi HospitalEarly P1C (39)
Biological Ntla-3001
Alpha 1-Antitrypsin Deficiency
Intellia TherapeuticsP1/2NR ()
ce1226
Alpha 1-Antitrypsin Deficiency
CSL BehringP4NR ()
Krro-110
Alpha 1-Antitrypsin Deficiency
Korro Bio, Inc.P1/2NR ()