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32 assets in Hematologic Disorder

Therapeutic assets addressing Hematologic Disorder, rated under Floatz methodology v0.2 and sorted by current rating.

AssetSponsorPhaseRating
Cyclophosphamide
Hematologic Disorder
Baptist Health South FloridaP2/3BBB (75)
Fludarabine
Hematologic Disorder
Baptist Health South FloridaP2BB (71)
Autologous Cd34+ Cells Isolated From Mobilised Peripheral Blood By Positive Selection, Modified By Crispr/Cas9 (Clustered Regularly Interspaced Short Palindromic Repeats/Crispr-Associated Protein 9) Mediated Gene Editing Consisting Of A Guide Rna (Grna) Introduced Transiently As Ribonucleoprotein (Rnp) Complex, Targeting The Erythroid Lineage-Specific Enhancer Region Of Bcl11A (B-Cell Lymphoma/Leukemia 11A). The Site-Specific Cleavage By Cas9 Forms A Double Strand Break (Dsb), Which Is Subsequently Repaired By Nonhomologous End-Joining (Nhej), Leading To The Transcriptional Repression Of Bcl11A, A Repressor Of ?-Globin Gene Transcription
Hematologic Disorder
Vertex Pharmaceuticals IncorporatedP3BB (70)
Busulfanum
Hematologic Disorder
Baptist Health South FloridaP2BB (69)
Lenalidomide
Hematologic Disorder
Hellenic Society of HematologyP3BB (68)
Dexasone
Hematologic Disorder
Hellenic Society of HematologyP2BB (67)
Tacrolimus
Hematologic Disorder
University of Michigan Rogel Cancer CenterP2BB (66)
Thiotepa
Hematologic Disorder
Baptist Health South FloridaP2BB (64)
Azacitidine
Hematologic Disorder
M.D. Anderson Cancer CenterP2B (60)
Melphalan
Hematologic Disorder
Baptist Health South FloridaP2B (60)
Pomalidomide
Hematologic Disorder
Hellenic Society of HematologyP2B (60)
Methotrexate
Hematologic Disorder
University of Michigan Rogel Cancer CenterP2B (59)
Bortezomib
Hematologic Disorder
Hellenic Society of HematologyP2CCC (53)
Brentuximab Vedotin
Hematologic Disorder
M.D. Anderson Cancer CenterP2CCC (53)
Isatuximab
Hematologic Disorder
Hellenic Society of HematologyP2CCC (53)
Ranitidine
Hematologic Disorder
Hellenic Society of HematologyP2CCC (53)
Venetoclax
Hematologic Disorder
M.D. Anderson Cancer CenterP2CCC (53)
Daratumumab
Hematologic Disorder
Anaveon AGP1/2CCC (52)
Diphenhydramine
Hematologic Disorder
Hellenic Society of HematologyP2CCC (51)
Belantamab Mafodotin
Hematologic Disorder
Hellenic Society of HematologyP1/2CCC (48)
rd13-02 cell infusion
Hematologic Disorder
Kai Lin Xu,MDEarly P1CC (47)
Vorinostat
Hematologic Disorder
University of Michigan Rogel Cancer CenterP1/2CC (47)
Nirogacestat
Hematologic Disorder
Hellenic Society of HematologyP1/2CC (45)
anv419
Hematologic Disorder
Anaveon AGP1CC (43)
gsk4172239d
Hematologic Disorder
GlaxoSmithKlineP1CC (43)
Kln-1010
Hematologic Disorder
Kelonia Therapeutics, Inc.P1CC (43)
Oricar-017
Hematologic Disorder
OriCell Therapeutics Co., Ltd.P1CC (43)
Levetiracetam
Hematologic Disorder
Masonic Cancer Center, University of MinnesotaN/AD (30)