1 asset in Leber Congenital Amaurosis
Therapeutic assets addressing Leber Congenital Amaurosis, rated under Floatz methodology v0.2 and sorted by current rating.
| Asset | Sponsor | Phase | Rating |
|---|---|---|---|
Sepofarsen Leber Congenital Amaurosis | Laboratoires Thea | P3 | NR () |