1 asset in Pelizaeus-Merzbacher Spectrum Disorder
Therapeutic assets addressing Pelizaeus-Merzbacher Spectrum Disorder, rated under Floatz methodology v0.2 and sorted by current rating.
| Asset | Sponsor | Phase | Rating |
|---|---|---|---|
Duoc-01 Pelizaeus-Merzbacher Spectrum Disorder | Joanne Kurtzberg, MD | P1 | CC (43) |