1 asset in Systemic Primary Carnitine Deficiency Disease
Therapeutic assets addressing Systemic Primary Carnitine Deficiency Disease, rated under Floatz methodology v0.2 and sorted by current rating.
| Asset | Sponsor | Phase | Rating |
|---|---|---|---|
L Carnitine Systemic Primary Carnitine Deficiency Disease | Ain Shams University | Early P1 | NR () |