Therapeutic Asset Ratings
474 results matching 1 filter
133,990 assets · 8,802 sponsors · 3,128 indications
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Sponsor
Phase
Rating
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy
Novartis Pharmaceuticals
P4
A
(80)
Delandistrogene Moxeparvovec
Duchenne Muscular Dystrophy
Sarepta Therapeutics, Inc.
P3
BB
(70)
Rgx-121
Mucopolysaccharidosis Type II (MPS II)
REGENXBIO Inc.
P3
BB
(70)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy 1
Novartis Gene Therapies
P3
BB
(69)
csl222
Hemophilia B
CSL Behring
P3
BB
(67)
gc101
SMA - Spinal Muscular Atrophy
GeneCradle Inc
P3
BB
(66)
Pelareorep
Advanced or Metastatic Breast Cancer
Adlai Nortye Biopharma Co., Ltd.
P2
BB
(66)
Recombinant Human Adenovirus Type 5
Hepatocellular Carcinoma
Henan Cancer Hospital
P4
BB
(64)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type I
Novartis Gene Therapies
P3
BB
(64)
Valoctocogene Roxaparvovec
Hemophilia A
BioMarin Pharmaceutical
P3
BB
(64)
Vesemnogene Lantuparvovec
Spinal Muscular Atrophy
Lantu Biopharma
P3
BB
(64)
Imnn-001
Epithelial Ovarian Cancer
Imunon
P3
B
(63)
Imnn-001
Primary Peritoneal Cancer
Imunon
P3
B
(63)
Oncolytic Measles Virus Encoding Thyroidal Sodium Iodide Symporter
Platinum-Resistant Primary Peritoneal Carcinoma
Mayo Clinic
P2
B
(63)
ICP34.5-, ICP47-DELETED HERPES SIMPLEX VIRUS 1 (HSV-1) INCORPORATING THE HUMAN GM-CSF GENE
Melanoma
Amgen
P3
B
(62)
pf-06838435
Hemophilia B
Pfizer
P3
B
(62)
Sgt-003
Duchenne Muscular Dystrophy
Solid Biosciences Inc.
P3
B
(62)
Aav-Gad
Parkinson's Disease
MeiraGTx, LLC
P2
B
(61)
flt201
Gaucher Disease Type 1
Spur Therapeutics
P3
B
(60)
gc101 adeno-associated virus
SMA - Spinal Muscular Atrophy
GeneCradle Inc
P3
B
(60)
Imnn-001
Fallopian Tube Cancer
Imunon
P3
B
(60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophies
Novartis Pharmaceuticals
P3
B
(60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type II
Novartis Gene Therapies
P3
B
(60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type III
Novartis Gene Therapies
P3
B
(60)
Olvimulogene Nanivacirepvec
Endometrioid Ovarian Cancer
Genelux Corporation
P3
B
(60)
Showing 1 to 25 of 474 assets
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