Rgx-121
Mucopolysaccharidosis Type II (MPS II)
REGENXBIO Inc.gene_therapyPhase 3Active
BB
70/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 58/ 100
- Competitive Position
- 95/ 100
Competitive context
22 Active assets in the Mucopolysaccharidosis Type II (MPS II) cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
gc1111 Takeda | Phase 4 | A |
PABINAFUSP ALFA JCR Pharmaceuticals Co., Ltd. | Phase 3 | BBB |
Idursulfase Beta GC Biopharma Corp | Phase 3 | BBB |
IMMUNOGLOBULIN G 1 (HUMAN-MOUSE MONOCLONAL IDEC-C2B8 .GAMMA.1-CHAIN ANTI-HUMAN ANTIGEN CD 20), DISULFIDE WITH HUMAN-MOUSE MONOCLONAL IDEC-C2B8 .KAPPA.-CHAIN, DIMER Takeda | Phase 4 | BB |
Gnr-055 AO GENERIUM | Phase 2/3 | BB |
View all 32 →
Same molecule, other indications
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