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Therapeutic Asset Ratings

474 results matching 1 filter

133,990 assets · 8,802 sponsors · 3,128 indications
Methodology v0.2
AssetSponsorPhaseRating
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy
Novartis PharmaceuticalsP4A (80)
Delandistrogene Moxeparvovec
Duchenne Muscular Dystrophy
Sarepta Therapeutics, Inc.P3BB (70)
Rgx-121
Mucopolysaccharidosis Type II (MPS II)
REGENXBIO Inc.P3BB (70)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy 1
Novartis Gene TherapiesP3BB (69)
csl222
Hemophilia B
CSL BehringP3BB (67)
gc101
SMA - Spinal Muscular Atrophy
GeneCradle IncP3BB (66)
Pelareorep
Advanced or Metastatic Breast Cancer
Adlai Nortye Biopharma Co., Ltd.P2BB (66)
Recombinant Human Adenovirus Type 5
Hepatocellular Carcinoma
Henan Cancer HospitalP4BB (64)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type I
Novartis Gene TherapiesP3BB (64)
Valoctocogene Roxaparvovec
Hemophilia A
BioMarin PharmaceuticalP3BB (64)
Vesemnogene Lantuparvovec
Spinal Muscular Atrophy
Lantu BiopharmaP3BB (64)
Imnn-001
Epithelial Ovarian Cancer
ImunonP3B (63)
Imnn-001
Primary Peritoneal Cancer
ImunonP3B (63)
Oncolytic Measles Virus Encoding Thyroidal Sodium Iodide Symporter
Platinum-Resistant Primary Peritoneal Carcinoma
Mayo ClinicP2B (63)
ICP34.5-, ICP47-DELETED HERPES SIMPLEX VIRUS 1 (HSV-1) INCORPORATING THE HUMAN GM-CSF GENE
Melanoma
AmgenP3B (62)
pf-06838435
Hemophilia B
PfizerP3B (62)
Sgt-003
Duchenne Muscular Dystrophy
Solid Biosciences Inc.P3B (62)
Aav-Gad
Parkinson's Disease
MeiraGTx, LLCP2B (61)
flt201
Gaucher Disease Type 1
Spur TherapeuticsP3B (60)
gc101 adeno-associated virus
SMA - Spinal Muscular Atrophy
GeneCradle IncP3B (60)
Imnn-001
Fallopian Tube Cancer
ImunonP3B (60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophies
Novartis PharmaceuticalsP3B (60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type II
Novartis Gene TherapiesP3B (60)
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOTER (CBA)
Spinal Muscular Atrophy Type III
Novartis Gene TherapiesP3B (60)
Olvimulogene Nanivacirepvec
Endometrioid Ovarian Cancer
Genelux CorporationP3B (60)
Showing 1 to 25 of 474 assets
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