Ataluren
Duchenne Muscular Dystrophy
PTC TherapeuticsSmall moleculePhase 3Active
BB
64/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 55/ 100
- Competitive Position
- 81/ 100
Competitive context
55 Active assets in the Duchenne Muscular Dystrophy cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Viltolarsen NS Pharma, Inc. | Phase 4 | BBB |
Golodirsen Rare Disease Research, LLC | Phase 4 | BB |
Delandistrogene Moxeparvovec Sarepta Therapeutics, Inc. | Phase 3 | BB |
Aoc 1044 Avidity Biosciences, Inc. | Phase 3 | BB |
Glutamine Assistance Publique - Hôpitaux de Paris | Phase 3 | BB |
View all 50 →
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