IDURONIDASE, .ALPHA.-L-(8-HISTIDINE) (HUMAN)
Pompe Disease Infantile-Onset
University of California, San Franciscoprotein_peptidePhase 1Active
CC
43/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 28/ 100
- Competitive Position
- 95/ 100
Competitive context
4 Active assets in the Pompe Disease Infantile-Onset cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Alglucosidase Alfa Genzyme, a Sanofi Company | Phase 4 | BB |
Cipaglucosidase Alfa-ATGA Amicus Therapeutics | Phase 3 | B |
Miglustat Amicus Therapeutics | Phase 3 | B |
gc301 GeneCradle Inc | Phase 1/2 | CCC |
gc301 GeneCradle Inc | Phase 1/2 | CCC |
at2221 | D |
Same molecule, other indications
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