Miglustat
Glycogen Storage Disease Type II Infantile Onset
Amicus TherapeuticsSmall moleculePhase 3Active
B
60/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 45/ 100
- Competitive Position
- 95/ 100
Competitive context
4 Active assets in the Glycogen Storage Disease Type II Infantile Onset cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Alglucosidase Alfa Genzyme, a Sanofi Company | Phase 4 | BB |
Cipaglucosidase Alfa-ATGA Amicus Therapeutics | Phase 3 | B |
gc301 GeneCradle Inc | Phase 1/2 | CCC |
gc301 GeneCradle Inc | Phase 1/2 | CCC |
IDURONIDASE, .ALPHA.-L-(8-HISTIDINE) (HUMAN) University of California, San Francisco | Phase 1 | CC |
at2221 | D |
Same molecule, other indications
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