Plozasiran
Familial Chylomicronemia
Arrowhead Pharmaceuticalsnucleic_acidPhase 3Active
BB
69/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 56/ 100
- Competitive Position
- 95/ 100
Competitive context
2 Active assets in the Familial Chylomicronemia cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
lcq908 Novartis Pharmaceuticals | Phase 3 | BB |
Volanesorsen Akcea Therapeutics | Phase 3 | B |
VUPANORSEN Akcea Therapeutics | Phase 2 | B |
Orlistat University of Texas Southwestern Medical Center | Phase 2 | CCC |
Slx-4090 University of Texas Southwestern Medical Center | Phase 2 | CCC |
rn0361 Ikaria Bioscience Pty Ltd | Phase 1/2 | CCC |
cs-121 CorrectSequence Therapeutics Co., Ltd | Early Phase 1 | C |
Olezarsen | D |
Same molecule, other indications
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