rn0361
Familial Chylomicronemia Syndrome
Ikaria Bioscience Pty LtdPhase 1/2Active
CCC
48/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 33/ 100
- Competitive Position
- 95/ 100
Competitive context
2 Active assets in the Familial Chylomicronemia Syndrome cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Plozasiran Arrowhead Pharmaceuticals | Phase 3 | BB |
lcq908 Novartis Pharmaceuticals | Phase 3 | BB |
Volanesorsen Akcea Therapeutics | Phase 3 | B |
VUPANORSEN Akcea Therapeutics | Phase 2 | B |
Slx-4090 University of Texas Southwestern Medical Center | Phase 2 | CCC |
Orlistat University of Texas Southwestern Medical Center | Phase 2 | CCC |
cs-121 CorrectSequence Therapeutics Co., Ltd | Early Phase 1 | C |
Olezarsen | D |
Same molecule, other indications
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